Biomarin International Limited
SpainAll drugs from this manufacturer
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It is used to treat patients with neuronal ceroid lipofuscinosis type 2 (NCL2), also known as tripeptidyl-peptidase 1 (TPP1) deficiency. It helps reduce the accumulation of materials in the body, especially in the brain, to delay the progression of the disease.
Dosage form: solution for infusion
Active substance Dosage cerliponase alfa 150 mg/ml -
It is used to treat hyperphenylalaninemia (HPA) or phenylketonuria (PKU), as well as BH4 deficiency, by helping to reduce phenylalanine levels in the blood.
Dosage form: tablets
Active substance Dosage sapropterin 100 mg -
It is used to treat patients with MPS VI (Mucopolysaccharidosis VI), a disease caused by the deficiency of a specific enzyme that leads to the accumulation of certain substances in the body's tissues.
Dosage form: solution for injection
Active substance Dosage galsulfase 1 mg -
It is used to treat adults and children with mucopolysaccharidosis type IVA (also known as Morquio A syndrome). This medication helps replace an enzyme that is missing in the body, which can improve walking and reduce the levels of certain substances that accumulate in the tissues.
Dosage form: solution for infusion, concentrate
Active substance Dosage elosulfase alfa 5 mg -
It is used to treat achondroplasia in patients from 4 months of age and older whose bones are still growing. This is a genetic disease that affects the growth of almost all the bones in the body.
Dosage form: powder and solution for injection
Active substance Dosage vosoritide 0,4 mg -
It is used to treat achondroplasia in patients from 4 months of age and older whose bones are still growing. This genetic disease affects the growth of almost all the bones in the body.
Dosage form: powder and solution for injection
Active substance Dosage vosoritide 0,56 mg -
It is used to treat achondroplasia in patients aged 4 months or older whose bones are still growing. This genetic disease affects the growth of nearly all the bones in the body.
Dosage form: powder and solution for injection
Active substance Dosage vosoritide 1,2 mg