Dipharma Arzneimittel GmbH
ItalyAll drugs from this manufacturer
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It is used to treat mild to moderate type 1 Gaucher disease in adults (if the patient cannot follow enzyme replacement therapy) and to treat progressive neurological symptoms in type C Niemann-Pick disease in adults and children.
Dosage form: capsules, hard gelatin
Active substance Dosage miglustat - ATC: A16AX06
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It is used for the treatment of hereditary tyrosinemia type 1 in adults, adolescents, and children of any age. The drug blocks the degradation of tyrosine, preventing the formation of harmful substances that accumulate in the body.
Dosage form: capsules, hard gelatin
Active substance Dosage nitisinone - ATC: A16AX04
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It is used to treat hyperphenylalaninemia (HPA), phenylketonuria (PKU), and BH4 deficiency, helping to reduce phenylalanine levels in the blood.
Dosage form: tablets, soluble
Active substance Dosage sapropterin dihydrochloride - ATC: A16AX07