miglustat

This medicine is used to treat type 1 Gaucher disease (mild to moderate) in adults, when enzyme replacement therapy cannot be used. It is also used to treat progressive neurological symptoms in Niemann-Pick disease type C in adults and children.

Form: capsules, hard gelatin

ATC: A16AX06

Manufacturer: ACCORD HEALTHCARE, S.L.U.

It is used to treat mild to moderate type 1 Gaucher disease in adults (if the patient cannot follow enzyme replacement therapy) and to treat progressive neurological symptoms in type C Niemann-Pick disease in adults and children.

Form: capsules, hard gelatin

ATC: A16AX06

Manufacturer: Dipharma Arzneimittel GmbH

It is used to treat type 1 Gaucher disease (mild to moderate) in adults when the patient is not suitable for enzyme replacement therapy, and to treat the progressive neurological symptoms of type C Niemann-Pick disease in adults and children.

Form: capsules, hard gelatin

ATC: A16AX06

Manufacturer: GEN.ORPH

Opfolda is used for the treatment of late-onset Pompe disease in adults. It is always used in conjunction with another medicine called cipaglucosidase alfa.

Form: capsules, hard gelatin

ATC: A16AX06

Manufacturer: AMICUS THERAPEUTICS EUROPE LIMITED

It is used to treat mild to moderate type 1 Gaucher disease in adults (if the patient cannot undergo enzyme replacement therapy) and to treat progressive neurological symptoms in type C Niemann-Pick disease in adults and children.

Form: capsules, hard gelatin

ATC: A16AX06

Manufacturer: PIRAMAL CRITICAL CARE B.V.

Zavesca is used to treat mild to moderate type 1 Gaucher disease in adults (if the patient cannot undergo enzyme replacement therapy) and to treat progressive neurological symptoms in type C Niemann-Pick disease in adults and children.

Form: capsules, hard gelatin

ATC: A16AX06

Manufacturer: JANSSEN-CILAG INTERNATIONAL N.V.