autologous cd34+ cell enriched cellular fraction containing genetically modified cd34+ cells with a retroviral vector containing the cdna sequence encoding human adenosine deaminase (ada)

Italy

Drugs containing this active substance

  • STRIMVELIS

    Strimvelis is a gene therapy used in children to treat a serious condition called ADA-SCID (adenosine deaminase deficiency severe combined immunodeficiency), which prevents the immune system from functioning correctly.

    Form: solution for infusion

    Active substance Dosage
    autologous cd34+ cell enriched cellular fraction containing genetically modified cd34+ cells with a retroviral vector containing the cdna sequence encoding human adenosine deaminase (ada) -

    ATC: L03AX

    Manufacturer: FONDAZIONE TELETHON ETS