FONDAZIONE TELETHON ETS

Italy

All drugs from this manufacturer

STRIMVELIS

Strimvelis is a gene therapy used in children to treat a serious condition called ADA-SCID (adenosine deaminase deficiency severe combined immunodeficiency), which prevents the immune system from functioning correctly.

Dosage form: solution for infusion

Active substance	Dosage
autologous cd34+ cell enriched cellular fraction containing genetically modified cd34+ cells with a retroviral vector containing the cdna sequence encoding human adenosine deaminase (ada)	-

ATC: L03AX