Genzyme Ireland Limited (manufacturing of the final product (filling, lyophilization), packaging, labeling, quality control and batch release, analytical testing of intermediate and finished medicinal products, stability testing, storage)

The drug is used for enzyme replacement therapy in children and adults with acid sphingomyelinase deficiency (ASM deficiency) type A/B or B, which is not accompanied by central nervous system manifestations.

Dosage form: powder for preparation of concentrate for infusion solution

ATC: A16AB25