ORCHARD THERAPEUTICS (NETHERLANDS) B.V.

Italy

All drugs from this manufacturer

  • LIBMELDY

    Libmeldy is a gene therapy used to treat metachromatic leukodystrophy (MLD) in children with 'late infantile' or 'early juvenile' forms who have not yet shown symptoms, or in children with the 'early juvenile' form who have begun to show symptoms but are not deteriorating rapidly.

    Dosage form: solution for infusion

    Active substance Dosage
    autologous cd34+ cells encoding the arsa gene -

    ATC: A16AB21