Amicus Therapeutics Europe Limited
SpainAll drugs from this manufacturer
-
It is used for the long-term treatment of Fabry disease in adults and adolescents aged 12 years or older who have certain genetic mutations.
Dosage form: capsules, hard
Active substance Dosage migalastat hydrochloride 150 mg -
It is used for the treatment of late-onset Pompe disease in adults, always in combination with another medication called cipaglucosidase alfa.
Dosage form: capsules, hard
Active substance Dosage miglustat 65 mg -
It is used in adults with late-onset Pompe disease. It works by helping to break down the glycogen that accumulates in the muscles due to the lack of a specific enzyme.
Dosage form: powder for concentrate for solution for infusion
Active substance Dosage cipaglucosidase alfa 105 mg