onasemnogen abeparvovec
UkraineDrugs containing this active substance
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The drug is intended for gene therapy in children up to 2 years of age with spinal muscular atrophy (SMA) caused by mutations in the SMN1 gene.
Form: suspension, for intravenous infusion
Active substance Dosage onasemnogen abeparvovec 2 x 10^13 vg/ml ATC: M09AX09
Manufacturer: Novartis Gene Therapies, Inc. (manufacturing, primary packaging, partial quality control, secondary packaging, batch release)