eladocagene exuparvovec
ItalyDrugs containing this active substance
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Upstaza is used for the treatment of patients aged 18 months and older presenting with aromatic L-amino acid decarboxylase (AADC) deficiency, a hereditary condition that can affect nervous system development, movement, feeding, breathing, speech, and mental abilities.
Form: solution for infusion
Active substance Dosage eladocagene exuparvovec - ATC: A16AB26
Manufacturer: PTC THERAPEUTICS INTERNATIONAL LIMITED